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Access to orphan drugs in western Europe: can more systematic policymaking really help to avoid different decisions

Tim A Kanters1, Leona Hakkaart, Maureen Pmh Rutten-van Mölken

  • 1Institute for Medical Technology Assessment, Erasmus University Rotterdam, PO Box 1738, 3000DR Rotterdam, The Netherlands.

Expert Review of Pharmacoeconomics & Outcomes Research
|May 15, 2015
PubMed

Keywords:
Pompe diseaseaccessmulti-criteria decision analysisorphan drugsreimbursement

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