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Applying genetics in inflammatory disease drug discovery
Lasse Folkersen1, Shameek Biswas2, Klaus Stensgaard Frederiksen3
1Department of PharmacoGenetics, Novo Nordisk, Novo Nordisk Park, Måløv, Denmark; Department of Integrative Systems Biology, Center for Biological Sequence Analysis, DTU, Lyngby, Denmark.
Abstract:
Recent groundbreaking work in genetics has identified thousands of small-effect genetic variants throughout the genome that are associated with almost all major diseases. These genome-wide association studies (GWAS) are often proposed as a source of future medical breakthroughs. However, with several notable exceptions, the journey from a small-effect genetic variant to a functional drug has proven arduous, and few examples of actual contributions to drug discovery exist. Here, we discuss novel approaches of overcoming this hurdle by using instead public genetics resources as a pragmatic guide alongside existing drug discovery methods. Our aim is to evaluate human genetic confidence as a rationale for drug target selection.
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