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Updated: Apr 5, 2026

Fingerprinting Cardiolipin in Leukocytes by Mass Spectrometry for a Rapid Diagnosis of Barth Syndrome
Published on: March 23, 2022
Nuria C Bramswig1, C W Ockeloen2, J C Czeschik3
1Institut für Humangenetik, Universitätsklinikum Essen, Universität Duisburg-Essen, Hufelandstr. 55, 45122, Essen, Germany. nuria.braemswig@uni-due.de.
Mutations in KCNH1 cause Temple-Baraitser syndrome (TMBTS) and Zimmermann-Laband syndrome (ZLS), with significant variability in symptoms like intellectual disability and nail hypoplasia. This study expands the known KCNH1 mutation spectrum, highlighting broader phenotypic presentation.
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