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Gene therapy in monogenic congenital myopathies

Xuan Guan1, Melissa A Goddard1, David L Mack2

  • 1Department of Physiology and Pharmacology, School of Medicine, Wake Forest University Health Sciences, Winston-Salem, NC, USA; Department of Rehabilitation Medicine, University of Washington, Seattle, WA, USA; Institute for Stem Cell and Regenerative Medicine, University of Washington, Seattle, WA, USA.

Methods (San Diego, Calif.)
|October 11, 2015
PubMed

Keywords:
Animal modelsGene therapyMuscle diseaseMuscular dystrophyMyopathy

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