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RNA Interference (RNAi)-Based Therapeutics: Delivering on the Promise?

Maggie L Bobbin1,2, John J Rossi3

  • 1Molecular Pathology Unit and.

Annual Review of Pharmacology and Toxicology
|January 8, 2016
PubMed
Summary

RNA interference (RNAi) therapeutics show promise, with over 20 in clinical trials. Advances in delivery and chemistry have overcome earlier challenges, paving the way for potential clinical approval.

Keywords:
clinical trialsdsiRNAmiRNAshRNAsiRNA

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