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Updated: Mar 21, 2026

Multi-exon Skipping Using Cocktail Antisense Oligonucleotides in the Canine X-linked Muscular Dystrophy
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The calpain-suppressing effects of olesoxime in Huntington's disease

Jonasz J Weber1, Midea M Ortiz Rios1, Olaf Riess1

  • 1Institute of Medical Genetics and Applied Genomics, University of Tuebingen, Tuebingen, Germany; Centre for Rare Diseases, University of Tuebingen, Tuebingen, Germany.

Rare Diseases (Austin, Tex.)
|May 4, 2016
PubMed

Keywords:
BACHD ratHdhQ111 knock-in mouseHuntington's diseasecalpainhuntingtin fragmentsmutant huntingtin aggregatesneurodegenerationolesoximepolyglutamine diseasesproteolysis

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