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Investor Outlook: Rising from the Ashes; GSK's European Approval of Strimvelis for ADA-SCID
Joshua Schimmer1, Steven Breazzano1
1Piper Jaffray & Co., New York, New York.
Human Gene Therapy. Clinical Development
|June 9, 2016
Abstract:
GlaxoSmithKline's (GSK) and partner San Raffaele Telethon Institute for Gene Therapy's recent positive European approval for Strimvelis for treatment of severe combined immunodeficiency due to adenosine deaminase deficiency (ADA-SCID) represents the second EU-approved gene therapy and the first γ-retrovirus and first ex vivo gene therapy. In this article we discuss the significance and implications of this historic approval for the broader gene therapy field.