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Forskolin-induced Swelling in Intestinal Organoids: An In Vitro Assay for Assessing Drug Response in Cystic Fibrosis Patients
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New Therapeutic Approaches to Modulate and Correct Cystic Fibrosis Transmembrane Conductance Regulator

Thida Ong1, Bonnie W Ramsey2

  • 1Division of Pulmonary and Sleep Medicine, Department of Pediatrics, Seattle Children's Hospital, University of Washington, 4800 Sand Point Way Northeast, M/S OC.7.720, Seattle, WA 98105, USA.

Pediatric Clinics of North America
|July 30, 2016
PubMed

Keywords:
CFTR modulatorCorrectorPersonalized medicinePotentiatorTherapeutics

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