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Health-related quality of life in mucopolysaccharidosis: looking beyond biomedical issues

Christian J Hendriksz1,2, Kenneth I Berger3, Christina Lampe4

  • 1Adult Inherited Metabolic Disorders, Consultant Transitional Metabolic Medicine, The Mark Holland Metabolic Unit, Salford Royal NHS Foundation Trust, Ladywell NW2- 2nd Floor Room 112, Salford, Manchester, M6 8HD, UK. cfya@sky.com.

Orphanet Journal of Rare Diseases
|August 27, 2016
PubMed

Keywords:
ADLClinical trialEQ-5DEnzyme replacement therapyHRQoLMPS HAQMucopolysaccharidosesPain measurementQuality of life

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