Differentiation of human and murine induced pluripotent stem cells to microglia-like cells

Hetal Pandya1, Michael J Shen1, David M Ichikawa1

  • 1National Institute of Neurological Disorders and Stroke, National Institutes of Health, Bethesda, Maryland, USA.

Nature Neuroscience
|March 3, 2017
PubMed

Insights

Researchers differentiated human induced pluripotent stem cells (iPSC) into microglia. These lab-grown microglia mimic human brain cells, paving the way for new CNS disease treatments and personalized medicine.

Area of Science:

  • Neuroscience
  • Stem Cell Biology
  • Immunology

Background:

  • Microglia, the resident immune cells of the central nervous system (CNS), are crucial for brain development, homeostasis, and neurological disease pathology.
  • Limited availability of human microglia hinders research and the clinical application of microglia-based therapies.
  • Existing microglia research heavily relies on animal models, which may not fully translate to human conditions.

Purpose of the Study:

  • To develop a reliable method for generating human microglia-like cells from induced pluripotent stem cells (iPSC).
  • To characterize the phenotype, gene expression, and functionality of these iPSC-derived microglia.
  • To assess the therapeutic potential of iPSC-derived microglia in a preclinical cancer model.

Main Methods:

  • Human iPSCs were differentiated into microglia-like cells through exposure to specific growth factors and co-culture with astrocytes.
  • Phenotypic, transcriptomic, and functional analyses were performed to compare iPSC-derived microglia with primary human microglia.
  • Murine iPSC-derived microglia were tested for efficacy in treating intracranial malignant gliomas in a syngeneic mouse model.

Main Results:

  • Successful differentiation of human iPSCs into microglia-like cells with characteristics mirroring primary human microglia.
  • iPSC-derived microglia exhibited comparable phenotype, gene expression profiles, and functional properties to their primary counterparts.
  • Murine iPSC-derived microglia demonstrated efficacy in treating brain tumors, similar to primary microglia.

Conclusions:

  • The generation of human microglia from iPSCs provides a valuable tool for studying CNS diseases and microglia biology.
  • This advancement facilitates the investigation of microglia in various neurological and psychiatric conditions.
  • iPSC-derived microglia hold promise for future personalized medicine applications in treating CNS disorders.