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Genome Editing in Mammalian Cell Lines using CRISPR-Cas
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CRISPR-Cas Genome Surgery in Ophthalmology

James E DiCarlo1,2, Jesse D Sengillo1,2,3, Sally Justus1,2

  • 1Jonas Children's Vision Care, and Bernard & Shirlee Brown Glaucoma Laboratory, Department of Ophthalmology, Columbia University, New York, NY, USA.

Translational Vision Science & Technology
|June 3, 2017
PubMed
Summary

Gene therapy using CRISPR-Cas tools offers new hope for genetic vision diseases. These advanced genome-editing technologies are revolutionizing ophthalmology research and treatment development.

Keywords:
CRISPR-Casgene therapygenome engineeringprecision medicinesynthetic biology

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