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Editorial: Clinical Trial Design for Alpha-1 Antitrypsin Deficiency: A Model for Rare Diseases

Michael R Jacobs1, Gerard J Criner1

  • 1Department of Thoracic Medicine and Surgery, Temple University School of Medicine, Philadelphia, Pennsylvania.

Chronic Obstructive Pulmonary Diseases (Miami, Fla.)
|August 30, 2017
PubMed
Abstract

No abstract available in PubMed .

Keywords:
alpha-1 antitrypsin deficiencyclinical trial designrare diseases: adaptive clinical trialssurrogate endpoints

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