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A novel nonviral gene delivery system for treating Leber's congenital amaurosis

Da Sun1, Rebecca M Schur1, Zheng-Rong Lu1,2

  • 1Case Center for Biomolecular Engineering, Department of Biomedical Engineering, School of Engineering, Case Western Reserve University, Cleveland, OH 44106, USA.

Therapeutic Delivery
|September 26, 2017
PubMed
Abstract

No abstract available in PubMed .

Keywords:
ECOLCARPE65gene therapynanoparticlenonviralretina

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