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The Dilemma of Two Innovative Therapies for Spinal Muscular Atrophy

Ans T van der Ploeg1

  • 1From the Center for Lysosomal and Metabolic Diseases, Erasmus University Medical Center, Rotterdam, the Netherlands.

The New England Journal of Medicine
|November 2, 2017
PubMed
Abstract

No abstract available in PubMed .

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