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Retinal Gene Therapy for Choroideremia: In Vitro Testing for Gene Augmentation Using an Adeno-Associated Viral (AAV)

Maria I Patrício1,2, Robert E MacLaren3,4,5

  • 1Nuffield Laboratory of Ophthalmology, Nuffield Department of Clinical Neurosciences, University of Oxford, Oxford, UK. enquiries@eye.ox.ac.uk.

Methods in Molecular Biology (Clifton, N.J.)
|December 1, 2017
PubMed

Keywords:
AAVChoroideremiaGene augmentationGene therapyHuman REP1Western blot

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