Functional rescue of misfolding ABCA3 mutations by small molecular correctors

Susanna Kinting1, Stefanie Höppner1, Ulrike Schindlbeck1

  • 1Department of Pediatric Pneumology, Dr. von Hauner Children's Hospital, Ludwig-Maximilians University, German Centre for Lung Research (DZL), 80337 Munich, Germany.

Human Molecular Genetics
|January 12, 2018
PubMed

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