Activation of Frataxin Protein Expression by Antisense Oligonucleotides Targeting the Mutant Expanded Repeat

Liande Li1,2, Xiulong Shen1,2, Zhongtian Liu1,2

  • 11 Department of Pharmacology, UT Southwestern Medical Center at Dallas , Dallas, Texas.

Nucleic Acid Therapeutics
|January 18, 2018
PubMed

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