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Multi-exon Skipping Using Cocktail Antisense Oligonucleotides in the Canine X-linked Muscular Dystrophy
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Antisense oligonucleotides and other genetic therapies made simple

Alexander M Rossor1,2, Mary M Reilly1, James N Sleigh2

  • 1MRC Centre for Neuromuscular Diseases, UCL Institute of Neurology and the National Hospital for Neurology and Neurosurgery, London, UK.

Practical Neurology
|February 19, 2018
PubMed

Keywords:
Rna interferenceantisense oligonucleotidesgenome editingneurogeneticsviral gene therapy

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