Gene therapy for visual loss: Opportunities and concerns

Jia Hui Lee1, Jiang-Hui Wang2, Jinying Chen3

  • 1Centre for Eye Research Australia, Royal Victorian Eye and Ear Hospital, East Melbourne, Victoria, Australia.

Summary

Gene therapy offers a genetic cure for disabling diseases, with recent advancements like CRISPR/Cas enabling precise genome engineering for ocular conditions. This review explores current gene therapy approaches, challenges, and future prospects for eye diseases.

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