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Updated: Feb 5, 2026

Multi-exon Skipping Using Cocktail Antisense Oligonucleotides in the Canine X-linked Muscular Dystrophy
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Exon Skipping by Ultrasound-Enhanced Delivery of Morpholino with Bubble Liposomes for Myotonic Dystrophy Model Mice

Yoichi Negishi1, Yoko Endo-Takahashi2, Shoichi Ishiura3

  • 1Department of Drug Delivery and Molecular Biopharmaceutics, School of Pharmacy, Tokyo University of Pharmacy and Life Sciences, Hachioji, Tokyo, Japan. negishi@toyaku.ac.jp.

Methods in Molecular Biology (Clifton, N.J.)
|September 2, 2018
PubMed

Keywords:
Antisense oligonucleotidesBubble liposomeExon skippingMyotonic dystrophy type 1 (DM1)PMOUltrasound

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