Chemically modified hCFTR mRNAs recuperate lung function in a mouse model of cystic fibrosis

A K M Ashiqul Haque1, Alexander Dewerth1, Justin S Antony1,2

  • 1Department of Pediatrics I - Pediatric Infectiology and Immunology, Translational Genomics and Gene Therapy, University of Tuebingen, Tuebingen, Germany.

Scientific Reports
|November 15, 2018
PubMed

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