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Making gene editing a therapeutic reality

Irina Conboy1, Niren Murthy1, Jessy Etienne1

  • 1Bioengineering, UC Berkeley, Berkeley, CA, 94720, USA.

F1000Research
|January 8, 2019
PubMed

Keywords:
AAVAlpha1 Antitrypsin deficiencyCRISPRClinical trialsDMDDNA damageHDRMyotonic DystrophyNHEJnanoparticles

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