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Updated: Jan 24, 2026

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Feasibility of using NF1-GRD and AAV for gene replacement therapy in NF1-associated tumors

Ren-Yuan Bai1, Dominic Esposito2, Ada J Tam3

  • 1Department of Neurosurgery, Johns Hopkins University School of Medicine, Baltimore, MD, USA. rbai1@jhmi.edu.

Gene Therapy
|May 26, 2019
PubMed

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