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Gene therapy for neurological disorders: challenges and recent advancements

Stefanie A Pena1, Rahul Iyengar1, Rebecca S Eshraghi1

  • 1Department of Otolaryngology, Hearing Research Laboratory, University of Miami Miller School of Medicine, Miami, FL, USA.

Journal of Drug Targeting
|June 15, 2019
PubMed

Keywords:
Autism Spectrum disorderCRISPER/Cas9 systemGene therapygene deliveryneurological diseasesnon-viral vectorsviral vectors

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