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Published on: August 20, 2019
Functionalization of CD36 cardiovascular disease and expression associated variants by interdisciplinary high
Namrata Madan1, Andrew R Ghazi2, Xianguo Kong1
1Cardeza Foundation for Hematologic Research/Department of Medicine, Sidney Kimmel Medical School, Thomas Jefferson University, Philadelphia, PA, United States of America.
Insights
Researchers identified a genetic variant regulating CD36 expression, impacting platelet function and cardiovascular disease risk. This discovery offers new avenues for precision medicine and patient management strategies.
Area of Science:
- Genetics
- Molecular Biology
- Cardiovascular Research
Background:
- CD36 is a platelet glycoprotein involved in oxidized low-density lipoprotein (oxLDL) binding and platelet activation.
- Genome-wide association studies link CD36 gene variants to platelet count, volume, lipid levels, and cardiovascular disease (CVD) risk.
- Platelet CD36 expression is associated with oxLDL response and thrombo-embolism risk, but causative variants remain elusive.
Purpose of the Study:
- To identify and functionally validate genetic variants that regulate platelet CD36 expression.
- To investigate the impact of these variants on CD36 transcription and platelet function.
- To assess the clinical relevance of identified variants using large-scale genetic data.
Main Methods:
- Screening of 81 expression quantitative trait loci (eQTL) single nucleotide polymorphisms (SNPs) using Massively Parallel Reporter Assays (MPRA).
- Analysis of MPRA data with a novel Bayesian statistical method.
- Validation of transcriptional regulation using luciferase assays, electromobility shift assays, and CRISPR/Cas9 gene editing in cell lines.
- Assessment of clinical relevance using the PhenoScanner tool.
Main Results:
- Ten eQTLs showed significant allele-specific transcription shifts, located upstream of CD36 transcriptional start sites.
- rs2366739 and rs1194196 variants were confirmed to alter transcriptional regulation and DNA:protein binding.
- CRISPR/Cas9-mediated deletion of the regulatory locus upregulated CD36 transcription.
- PhenoScanner analysis reinforced the clinical relevance of the identified variants.
Conclusions:
- A novel genetic variant regulating CD36 expression and subsequent platelet function has been identified.
- This study establishes a generalizable method for functional testing of genetic variants.
- Findings support potential applications in patient management and precision therapy development for cardiovascular diseases.
Abstract:
CD36 is a platelet membrane glycoprotein whose engagement with oxidized low-density lipoprotein (oxLDL) results in platelet activation. The CD36 gene has been associated with platelet count, platelet volume, as well as lipid levels and CVD risk by genome-wide association studies. Platelet CD36 expression levels have been shown to be associated with both the platelet oxLDL response and an elevated risk of thrombo-embolism. Several genomic variants have been identified as associated with platelet CD36 levels, however none have been conclusively demonstrated to be causative. We screened 81 expression quantitative trait loci (eQTL) single nucleotide polymorphisms (SNPs) associated with platelet CD36 expression by a Massively Parallel Reporter Assay (MPRA) and analyzed the results with a novel Bayesian statistical method. Ten eQTLs located 13kb to 55kb upstream of the CD36 transcriptional start site of transcript ENST00000309881 and 49kb to 92kb upstream of transcript ENST00000447544, demonstrated significant transcription shifts between their minor and major allele in the MPRA assay. Of these, rs2366739 and rs1194196, separated by only 20bp, were confirmed by luciferase assay to alter transcriptional regulation. In addition, electromobility shift assays demonstrated differential DNA:protein complex formation between the two alleles of this locus. Furthermore, deletion of the genomic locus by CRISPR/Cas9 in K562 and Meg-01 cells results in upregulation of CD36 transcription. These data indicate that we have identified a variant that regulates expression of CD36, which in turn affects platelet function. To assess the clinical relevance of our findings we used the PhenoScanner tool, which aggregates large scale GWAS findings; the results reinforce the clinical relevance of our variants and the utility of the MPRA assay. The study demonstrates a generalizable paradigm for functional testing of genetic variants to inform mechanistic studies, support patient management and develop precision therapies.
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