Hemophilia Gene Therapy: New Development from Bench to Bed Side

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Updated: Jan 19, 2026

Preparation and Gene Modification of Nonhuman Primate Hematopoietic Stem and Progenitor Cells
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Preparation and Gene Modification of Nonhuman Primate Hematopoietic Stem and Progenitor Cells

Published on: February 15, 2019

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Xiao-Lu Guo1,2, Tsai-Hua Chung1,3, Yue Qin3

  • 1Geno-immune Medical Institute, Shenzhen, China.

Current Gene Therapy
|September 25, 2019
PubMed

Keywords:
Gene therapyhemophiliahemostasislentiviral vectornovel gene therapyrecessive disorder.

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