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Updated: Dec 29, 2025

Limbal Approach-Subretinal Injection of Viral Vectors for Gene Therapy in Mice Retinal Pigment Epithelium
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New perspectives in gene therapy for inherited disorders

Maria Pia Cicalese1,2, Alessandro Aiuti1,2,3

  • 1San Raffaele Telethon Institute for Gene Therapy (TIGET), San Raffaele Scientific Institute Milan, Milan, Italy.

Pediatric Allergy and Immunology : Official Publication of the European Society of Pediatric Allergy and Immunology
|February 5, 2020
PubMed

Keywords:
cancergene therapyimmunodeficiencyinherited disorders

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