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Updated: Dec 28, 2025

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[Gene-specific treatment approaches in muscle diseases]

Diana Lehmann Urban1, Ilka Schneider2

  • 1Neurologische Universitätsklinik, Universitäts- und Rehabilitationskliniken Ulm, Oberer Eselsberg 45, 89081, Ulm, Deutschland. diana.lehmann@rku.de.

Der Nervenarzt
|February 21, 2020
PubMed

Keywords:
Antisense oligonucleotideCell-based treatmentGene therapyMuscular dystrophy, DuchenneMyotonic dystrophy 1

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