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Updated: Dec 25, 2025

Pre-clinical Evaluation of Tyrosine Kinase Inhibitors for Treatment of Acute Leukemia
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Orphan drug clinical development

Olivier Blin1, Marie-Noelle Lefebvre1, Olivier Rascol2

  • 1Service de pharmacologie clinique et pharmacovigilance, Aix Marseille Univ, AP-HM, INSERM, Inst Neurosci Syst, 13005 Marseille, France; Orphandev-FCRIN, INSERM, 13005 Marseille, France.

Therapie
|April 6, 2020
PubMed

Keywords:
Clinical trialMarket authorizationOrphan drugsPatientRare diseases

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