A contemporary therapeutic approach to bone disease in beta-thalassemia - a review

Dimitrios Stefanopoulos1, Nikolaos A Papaioannou1, Athanassios G Papavassiliou2

  • 1Laboratory for Research of the Musculoskeletal System "Th. Garofalidis", KAT Hospital, National and Kapodistrian University of Athens, School of Medicine, Athens, Greece.

Insights

Beta-thalassemia patients face significant bone problems due to improved survival. This review details prevention and treatment strategies for thalassemia bone disease, including diet, lifestyle, and medical regimens.

Area of Science:

  • Hematology
  • Endocrinology
  • Metabolic Bone Disease

Background:

  • Homozygous beta-thalassemia survival has increased, leading to bone complications.
  • Thalassemia bone disease is a major issue in long-term survivors.
  • Etiology is multifactorial, differing from postmenopausal osteoporosis.

Purpose of the Study:

  • To review and synthesize data on preventing and treating thalassemia bone disease.
  • Focus on diet, lifestyle, hematologic management, and anti-osteoporosis treatments.
  • Provide a comprehensive overview of current knowledge.

Main Methods:

  • Systematic literature review using PubMed.
  • Focused on data from the last 29 years.
  • Included studies on prevention and treatment of thalassemia bone disease.

Main Results:

  • Bisphosphonates are a primary treatment with satisfactory results.
  • Emerging data supports denosumab and teriparatide.
  • Investigational therapies are in clinical trials.

Conclusions:

  • Thalassemia bone disease requires a multifactorial management approach.
  • Current treatments like bisphosphonates show efficacy.
  • New therapeutic agents offer future treatment possibilities.

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