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AAV5-miHTT gene therapy for Huntington disease: lowering both huntingtins

Melvin M Evers1, Pavlina Konstantinova1

  • 1Research, uniQure biopharma B.V , Amsterdam, The Netherlands.

Expert Opinion on Biological Therapy
|July 14, 2020
PubMed
Abstract

No abstract available in PubMed .

Keywords:
AAV5ASOHTTHuntington diseaseadeno-associated virusantisense oligonucleotidehuntingtin loweringmicroRNA

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