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A Review of Gene, Drug and Cell-Based Therapies for Usher Syndrome

Lucy S French1, Carla B Mellough1, Fred K Chen1,2,3

  • 1Centre for Ophthalmology and Visual Sciences (incorporating Lions Eye Institute), The University of Western Australia, Nedlands, WA, Australia.

Frontiers in Cellular Neuroscience
|August 1, 2020
PubMed

Keywords:
adeno-associated virusantisense oligonucleotidescell therapygene editinggene therapyipscsusher syndrome

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