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A Combined 3D Tissue Engineered In Vitro/In Silico Lung Tumor Model for Predicting Drug Effectiveness in Specific Mutational Backgrounds
Published on: April 6, 2016
Epigenetic Input Dictates the Threshold of Targeting of the Integrin-Dependent Pathway in Non-small Cell Lung Cancer
Yang Zhang1,2,3, Kai Cheng4, Bingwei Xu2,3
1Department of Respiratory Medicine, First Affiliated Hospital of Soochow University, Suzhou, China.
Abstract:
We investigated the therapeutic potential of targeting integrin/FAK-dependent signaling, an adhesion receptor-mediated pathway that has been increasingly linked to non-small cell lung cancer (NSCLC) malignancy. Our analysis of the TCGA cohort showed that a subset of pro-tumorigenic integrins, including α1β1, α2β1, α3β1, α5β1, and α6β4, were frequently amplified or upregulated at the genomic or mRNA level in KRAS or EGFR mutation/overexpression-enriched adenocarcinomas. These alterations appeared complementary, correlated with poor patient survival (p < 0.0072), and were collaborative with KRAS mutation-coupled αv integrins (p < 0.00159). Since integrin/FAK-dependent signaling is tightly coupled with normal human physiology, we sought to use a synthetic lethal-type targeting comprising of VS-6063, a chemical inhibitor of integrin-mediated FAK activity, and A549 cells, which carry a KRAS mutation and EGFR overexpression. Our screening analysis revealed that JQ1 and IBET-762, inhibitors of epigenetic reader BRD4, and LBH589, a pan inhibitor of histone deacetylases (HDACs), exhibited synergy with VS-6063 in mitigating tumor cell viability. This epigenetic link was corroborated by strong effects of additional inhibitors and RNAi-mediated knockdown of FAK and BRD4 or its downstream effector, c-Myc. Low doses of JQ1 (≤0.5 μM) markedly escalated efficacy of VS-6063 across a panel of 10 NSCLC cell lines. This catalyst-like effect is in line with the oncogenic landscape in the TCGA cohort since c-Myc falls downstream of the KRAS and EGFR oncogenes. Mechanistically, co-inhibiting the integrin-FAK and BRD4/c-Myc axes synergistically induced apoptotic cell death and DNA damage response, and impaired stemness-associated tumorsphere formation. These effects were accompanied by a marked inhibition of Akt- and p130Cas/Src-dependent signaling, but not Erk1/2 activity. Meanwhile, JQ1 alone or in combination with VS-6063 attenuated cell-cell adhesion and extracellular matrix (ECM)-dependent cell spreading, which is reminiscent of phenotype induced by malfunctional E-cadherin or integrins. Paradoxically, this phenotypic impact coincided with downregulation of epithelial-mesenchymal transition (EMT)-inducting transcription factor ZEB1 or Snail. Finally, we showed that the effect of the VS-6063/JQ1 combination was nearly equivalent to that of VS-6063 plus Carboplatin or Osimertinib. Overall, our study indicates that the integrin/FAK and BRD4/c-Myc axes cooperatively drive NSCLC virulence, and a co-targeting may provide a line of therapy capable of overcoming EGFR/KRAS-driven malignancy.
Insights
Targeting integrin/FAK and BRD4/c-Myc pathways simultaneously shows therapeutic potential for non-small cell lung cancer (NSCLC). This combination therapy, using VS-6063 and JQ1, synergistically reduces tumor cell viability and overcomes KRAS/EGFR-driven malignancy.
Area of Science:
- Oncology
- Molecular Biology
- Cancer Therapeutics
Background:
- Integrin/FAK signaling is implicated in non-small cell lung cancer (NSCLC) malignancy.
- Specific integrins (α1β1, α2β1, α3β1, α5β1, α6β4) are upregulated in KRAS/EGFR-driven NSCLC, correlating with poor survival.
- Targeting integrin/FAK signaling presents a potential therapeutic strategy, but requires careful consideration due to its role in normal physiology.
Purpose of the Study:
- To investigate the therapeutic potential of co-targeting integrin/FAK-dependent signaling and epigenetic pathways in NSCLC.
- To evaluate the synergistic effects of VS-6063 (integrin-mediated FAK inhibitor) with epigenetic modulators like JQ1 (BRD4 inhibitor) in NSCLC cells.
- To elucidate the molecular mechanisms underlying the combined therapeutic effects.
Main Methods:
- Analysis of TCGA cohort for integrin expression and correlation with patient survival in NSCLC.
- In vitro screening of NSCLC cell lines (A549) with VS-6063 in combination with epigenetic inhibitors (JQ1, IBET-762, LBH589).
- RNAi-mediated knockdown of FAK and BRD4/c-Myc.
- Assessment of synergistic effects on cell viability, apoptosis, DNA damage, stemness, signaling pathways (Akt, Src, Erk1/2), cell adhesion, and epithelial-mesenchymal transition (EMT).
Main Results:
- Upregulation of pro-tumorigenic integrins in KRAS/EGFR-mutated NSCLC, associated with poor prognosis.
- Synergistic reduction in tumor cell viability by combining VS-6063 with BRD4 inhibitors (JQ1, IBET-762) or HDAC inhibitors (LBH589).
- Low-dose JQ1 significantly enhanced VS-6063 efficacy across multiple NSCLC cell lines.
- Combined inhibition of integrin-FAK and BRD4/c-Myc axes induced apoptosis, DNA damage, impaired stemness, and modulated signaling pathways.
- The combination therapy showed comparable efficacy to standard treatments like Carboplatin or Osimertinib.
Conclusions:
- The integrin/FAK and BRD4/c-Myc axes cooperatively drive NSCLC progression.
- Combined targeting of these axes offers a promising therapeutic strategy for overcoming KRAS/EGFR-driven NSCLC.
- This co-targeting approach may provide a novel line of therapy for NSCLC patients.
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