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Patient reported outcome measures in a large cohort of patients with type 1 Gaucher disease

Tama Dinur1, Majdolen Istaiti1, Dafna Frydman1

  • 1Gaucher Unit, Shaare Zedek Medical Centre, P.O. Box 3235, 91031, Jerusalem, Israel.

Orphanet Journal of Rare Diseases
|October 14, 2020
PubMed
Abstract

Keywords:
Adult patientsGaucher diseaseMobile surveyPatients reported outcomeQuality of life

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