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Gene therapy in Duchenne muscular dystrophy: Identifying and preparing for the challenges ahead

Emma Heslop1, Cathy Turner1, Anna Irvin1

  • 1John Walton Muscular Dystrophy Research Centre, Translational and Clinical Research Institute, Newcastle University and Newcastle Hospitals NHS Foundation Trust, Newcastle upon Tyne, UK.

Neuromuscular Disorders : NMD
|November 7, 2020
PubMed
Abstract

No abstract available in PubMed .

Keywords:
BarriersCollaborationDuchenne muscular dystrophyGene therapy

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