You might also read
Articles linked to this work by shared authors, journal, and citation graph.
Updated: Nov 25, 2025

Systemic Delivery of MicroRNA Using Recombinant Adeno-associated Virus Serotype 9 to Treat Neuromuscular Diseases in Rodents
Published on: August 10, 2018
Kai-Chen Wang1,2, Chiao-Yuan Fang3, Chi-Chang Chang4
1Cheng-Hsin General Hospital, Taipei, Taiwan.
A new digital PCR method accurately detects spinal muscular atrophy (SMA) by analyzing survival motor neuron (SMN) gene copy numbers. This rapid test aids in early diagnosis for carriers and patients, improving genetic screening outcomes.
05:16Characterizing Exon Skipping Efficiency in DMD Patient Samples in Clinical Trials of Antisense Oligonucleotides
Published on: May 7, 2020
09:18Measurements of Motor Function and Other Clinical Outcome Parameters in Ambulant Children with Duchenne Muscular Dystrophy
Published on: January 12, 2019
Area of Science:
Background:
Purpose of the Study:
Main Methods:
Main Results:
Conclusions: