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Updated: Nov 24, 2025

Exploring Sequence Space to Identify Binding Sites for Regulatory RNA-Binding Proteins
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Clinical Applications of Single-Stranded Oligonucleotides: Current Landscape of Approved and In-Development

Juergen Scharner1, Isabel Aznarez1

  • 1Stoke Therapeutics, Inc., Bedford, MA, USA.

Molecular Therapy : the Journal of the American Society of Gene Therapy
|December 28, 2020
PubMed

Keywords:
CpG oligonucleotidesRNase Hantisense oligonucleotidesgapmersplicingsteric blocking

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