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Evaluating the Impact of Stopping Chronic Therapies after Modulator Drug Therapy in Cystic Fibrosis: The SIMPLIFY

Nicole Mayer-Hamblett1,2,3, David P Nichols1,2, Katherine Odem-Davis1

  • 1Cystic Fibrosis Therapeutics Development Network Coordinating Center, Seattle Children's Hospital, Seattle, Washington.

Annals of the American Thoracic Society
|January 19, 2021
PubMed

Keywords:
CFTR modulatorsnoninferiority trialtreatment burden

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