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Advances and Obstacles in Homology-Mediated Gene Editing of Hematopoietic Stem Cells

Christi T Salisbury-Ruf1, Andre Larochelle1

  • 1Cellular and Molecular Therapeutics Branch, National Heart, Lung and Blood Institute (NHLBI), National Institutes of Health (NIH), Bethesda, MD 20892, USA.

Journal of Clinical Medicine
|February 4, 2021
PubMed

Keywords:
AAV6CRISPR-Cas9gene editinghematopoietic stem and progenitor cellshomology-directed repair

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