Related Experiment Video
Updated: Nov 12, 2025

05:16
Characterizing Exon Skipping Efficiency in DMD Patient Samples in Clinical Trials of Antisense Oligonucleotides
Published on: May 7, 2020
7.1K
Molecular Diagnosis in 100% of Dystrophinopathies: Are We There Yet?
1ERN Neuromuscular Unit, Department of Neurosciences, DNS, University of Padova, Padova, Italy.
Neurology. Genetics
|March 17, 2021
Abstract
No abstract available in PubMed .

