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Antipsychotic drugs counteract autophagy and mitophagy in multiple sclerosis
Simone Patergnani1, Massimo Bonora1, Selene Ingusci2
1Department of Medical Sciences, Section of Experimental Medicine, Laboratory for Technologies of Advanced Therapies, University of Ferrara, 44121 Ferrara, Italy.
Abstract:
Multiple sclerosis (MS) is a neuroinflammatory and neurodegenerative disease characterized by myelin damage followed by axonal and ultimately neuronal loss. The etiology and physiopathology of MS are still elusive, and no fully effective therapy is yet available. We investigated the role in MS of autophagy (physiologically, a controlled intracellular pathway regulating the degradation of cellular components) and of mitophagy (a specific form of autophagy that removes dysfunctional mitochondria). We found that the levels of autophagy and mitophagy markers are significantly increased in the biofluids of MS patients during the active phase of the disease, indicating activation of these processes. In keeping with this idea, in vitro and in vivo MS models (induced by proinflammatory cytokines, lysolecithin, and cuprizone) are associated with strongly impaired mitochondrial activity, inducing a lactic acid metabolism and prompting an increase in the autophagic flux and in mitophagy. Multiple structurally and mechanistically unrelated inhibitors of autophagy improved myelin production and normalized axonal myelination, and two such inhibitors, the widely used antipsychotic drugs haloperidol and clozapine, also significantly improved cuprizone-induced motor impairment. These data suggest that autophagy has a causal role in MS; its inhibition strongly attenuates behavioral signs in an experimental model of the disease. Therefore, haloperidol and clozapine may represent additional therapeutic tools against MS.
Insights
Autophagy and mitophagy are elevated in active multiple sclerosis (MS). Inhibiting these processes, using drugs like haloperidol and clozapine, improved myelin repair and motor function in MS models.
Area of Science:
- Neuroscience
- Cell Biology
- Immunology
Background:
- Multiple sclerosis (MS) is a chronic neuroinflammatory and neurodegenerative disease.
- Current MS therapies lack complete efficacy, and its exact causes remain unclear.
- Autophagy and mitophagy are crucial cellular degradation pathways implicated in various diseases.
Purpose of the Study:
- To investigate the role of autophagy and mitophagy in the pathogenesis of multiple sclerosis.
- To explore whether modulating these pathways can offer therapeutic benefits for MS.
Main Methods:
- Assessed autophagy and mitophagy markers in biofluids from MS patients during active disease phases.
- Utilized in vitro and in vivo experimental models of MS induced by various agents.
- Administered structurally diverse autophagy inhibitors, including haloperidol and clozapine, to MS models.
Main Results:
- Autophagy and mitophagy markers were significantly elevated in active MS patients.
- MS models exhibited impaired mitochondrial function, increased lactic acid metabolism, and heightened autophagic flux.
- Autophagy inhibition led to improved myelin production, normalized axonal myelination, and ameliorated motor deficits in experimental models.
Conclusions:
- Autophagy plays a causal role in multiple sclerosis.
- Inhibiting autophagy, particularly with haloperidol and clozapine, demonstrates therapeutic potential for MS by promoting myelin repair and improving neurological function.
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