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Clinical Perspectives of Gene-Targeted Therapies for Epidermolysis Bullosa

Tobias Welponer1, Christine Prodinger1, Josefina Pinon-Hofbauer1

  • 1Department of Dermatology and Allergology and EB House Austria, University Hospital of the Paracelsus Medical University, Salzburg, Austria.

Dermatology and Therapy
|June 10, 2021
PubMed

Keywords:
Antisense oligonucleotidesEpidermolysis bullosaGene editingGene replacementGene therapyReadthroughTrans-splicingsiRNA

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