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Updated: Oct 25, 2025

Preparation of Neutrally-charged, pH-responsive Polymeric Nanoparticles for Cytosolic siRNA Delivery
Published on: May 2, 2019
Clinical Advances of siRNA-Based Nanotherapeutics for Cancer Treatment
Dima Hattab1, Amirah Mohd Gazzali2, Athirah Bakhtiar3
1Faculty of Pharmacy, University of Jordan, Queen Rania Street, Amman 11942, Jordan.
Abstract:
Cancer is associated with single or multiple gene defects. Recently, much research has focused on incorporating genetic materials as one of the means to treat various types of carcinomas. RNA interference (RNAi) conveys an alternative genetic approach for cancer patients, especially when conventional medications fail. RNAi involves the inhibition of expression of specific messenger RNA that signals for uncontrollable cell growth and proliferation, most notably with carcinoma cells. This molecular technology is promising as genetic materials allow us to overcome issues associated with chemotherapeutic agents including organ damage associated with severe drug toxicities. Nonetheless, vast challenges impede successful gene therapy application, including low tumor localization, low stability and rapid clearance from the blood circulation. Owing to the limited treatment opportunities for the management of cancer, the development of effective siRNA carrier systems involving nanotherapeutics has been extensively explored. Over the past years, several siRNA nanotherapeutics have undergone a period of clinical investigation, with some demonstrating promising antitumor activities and safety profiles. Extensive observation of siRNA-nanoparticles is necessary to ensure commercial success. Therefore, this review mainly focuses on the progress of siRNAs-loaded nanoparticles that have undergone clinical trials for cancer treatment. The status of the siRNA nanotherapeutics is discussed, allowing comprehensive understanding of their gene-mediated therapeutics.
Insights
RNA interference (RNAi) offers a novel genetic therapy for cancer, inhibiting genes driving tumor growth. siRNA nanotherapeutics show promise in clinical trials, overcoming chemotherapy limitations.
Area of Science:
- Oncology
- Molecular Biology
- Nanotechnology
Background:
- Cancer arises from genetic defects, prompting research into genetic material-based treatments.
- Conventional chemotherapy faces limitations due to organ damage and drug toxicities.
Purpose of the Study:
- To review the progress of small interfering RNA (siRNA)-loaded nanoparticles in clinical trials for cancer treatment.
- To assess the therapeutic potential and challenges of siRNA nanotherapeutics in oncology.
Main Methods:
- Focus on clinical trial data of siRNA-loaded nanoparticles for cancer therapy.
- Analysis of gene-mediated therapeutic strategies and nanocarrier systems.
Main Results:
- siRNA nanotherapeutics demonstrate promising antitumor activities and safety profiles in clinical investigations.
- Challenges such as low tumor localization and rapid clearance persist.
Conclusions:
- siRNA-loaded nanoparticles represent a significant advancement in gene-mediated cancer therapy.
- Further observation and development are crucial for the commercial success of siRNA nanotherapeutics.
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