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Systemic Therapy for Lung Cancer Brain Metastases
Alessia Pellerino1, Francesco Bruno2, Roberta Rudà2,3
1Department of Neuro-Oncology, University and City of Health and Science Hospital, via Cherasco 15, 10126, Turin, Italy. alessia.pellerino85@gmail.com.
Opinion Statement:
Systemic therapy for brain metastases (BM) is quickly moving from conventional cytotoxic chemotherapy toward targeted therapies, that allow a disruption of driver molecular pathways. The discovery of actionable driver mutations has led to the development of an impressive number of tyrosine kinase inhibitors (TKIs), that target the epidermal growth factor receptor (EGFR) mutations, anaplastic-lymphoma-kinase (ALK) rearrangements, and other rare molecular alterations in patients bearing metastatic non-small cell lung cancer (NSCLC) in the brain, with remarkable results in terms of intracranial disease control and overall survival. Moreover, these drugs may delay the use of local therapies, such as stereotactic radiosurgery (SRS) or whole-brain radiotherapy (WBRT). New drugs with higher molecular specificity and ability to cross the CNS barriers (BBB, BTB and blood-CSF) are being developed. Two major issues are related to targeted therapies. First, the emergence of a resistance is a common event, and a deeper understanding of molecular pathways that are involved is critical for the successful development of effective new targeted agents. Second, an early detection of tumor progression is of utmost importance to avoid the prolongation of an ineffective therapy while changing to another drug. In order to monitor over time the treatment to targeted therapies, liquid biopsy, that allows the detection in biofluids of either circulating tumor cells (CTCs) or circulating tumor DNA (ctDNA) or exosomes, is increasingly employed in clinical trials: with respect to BM the monitoring of both blood and CSF is necessary. Also, radiomics is being developed to predict the mutational status of the BM on MRI.For patients without druggable mutations or who do not respond to targeted agents, immunotherapy with checkpoint inhibitors is increasingly employed, alone or in combination with radiotherapy. Pseudoprogression after immunotherapy alone maybe a challenge for several months after the start of treatment, and the same is true for radionecrosis after the combination of immunotherapy and SRS. In this regard, the value of advanced MRI techniques and PET imaging for a better distinction of pseudoprogression/radionecrosis and true tumor progression is promising, but needs validation in large prospective datasets. Last, a new frontier in the near future will be chemoprevention (primary and secondary), but we need to identify among solid tumors those subgroups of patients with a higher risk of relapsing into the brain and novel drugs, active on either neoplastic or normal cells of the microenvironment, that are cooperating in the invasion of brain tissue.
Insights
Systemic therapies for brain metastases are shifting towards targeted agents and immunotherapy, improving patient outcomes. Monitoring treatment response with liquid biopsies and advanced imaging is crucial for managing resistance and progression.
Area of Science:
- Oncology
- Neurology
- Pharmacology
Background:
- Systemic therapy for brain metastases (BM) is evolving from chemotherapy to targeted therapies and immunotherapy.
- Targeted therapies, including tyrosine kinase inhibitors (TKIs), show efficacy against specific mutations in non-small cell lung cancer (NSCLC) brain metastases.
- Immunotherapy with checkpoint inhibitors offers an alternative for patients without targetable mutations or who do not respond to targeted agents.
Purpose of the Study:
- To review the current landscape of systemic therapies for brain metastases.
- To discuss challenges and advancements in monitoring treatment response and managing resistance.
- To explore future directions in brain metastasis management, including chemoprevention.
Main Methods:
- Review of current literature on targeted therapies and immunotherapies for brain metastases.
- Discussion of diagnostic and monitoring tools such as liquid biopsy and advanced imaging.
- Exploration of emerging strategies like chemoprevention.
Main Results:
- Targeted therapies (TKIs) demonstrate significant intracranial disease control and improved survival in NSCLC BM.
- Liquid biopsy (ctDNA, CTCs, exosomes) and radiomics are emerging tools for monitoring treatment and predicting mutational status.
- Distinguishing pseudoprogression/radionecrosis from true progression requires advanced imaging techniques, necessitating further validation.
Conclusions:
- Targeted therapies and immunotherapy represent significant progress in managing brain metastases.
- Addressing resistance and accurately monitoring treatment response are critical for optimizing patient outcomes.
- Future research should focus on novel drug development, improved monitoring techniques, and chemoprevention strategies.
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