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Updated: Oct 15, 2025

Generation of Human Nasal Epithelial Cell Spheroids for Individualized Cystic Fibrosis Transmembrane Conductance Regulator Study
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Gene therapy for cystic fibrosis: new tools for precision medicine

Jin-A Lee1, Alex Cho2, Elena N Huang2

  • 1Program in Developmental and Stem Cell Biology, Hospital for Sick Children, 686 Bay Street, PGCRL 16-9420, Toronto, ON, M5G0A4, Canada.

Journal of Translational Medicine
|October 31, 2021
PubMed

Keywords:
Alternative chloride channelsCFTRCystic fibrosisLungOrganoidsPrecision medicineStem cellsTMEM16A

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