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Updated: Oct 14, 2025

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Characterizing Exon Skipping Efficiency in DMD Patient Samples in Clinical Trials of Antisense Oligonucleotides
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Correction to: Reldesemtiv in Patients with Spinal Muscular Atrophy: a Phase 2 Hypothesis-Generating Study
Stacy A Rudnicki1, Jinsy A Andrews1,2, Tina Duong3
1Cytokinetics, Incorporated, South San Francisco, CA, USA.
Abstract
No abstract available in PubMed .
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