RNA Splicing
Alternative RNA Splicing
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Updated: Oct 9, 2025

Engineering Artificial Factors to Specifically Manipulate Alternative Splicing in Human Cells
Published on: April 26, 2017
Carmelo Gurnari1,2, Simona Pagliuca1, Valeria Visconte1
1Department of Translational Hematology and Oncology Research, Taussig Cancer Institute, Cleveland Clinic, Cleveland, OH 44195, USA.
Alternative RNA splicing (AS) diversifies proteins and is vital for development. Dysregulation of AS contributes to myeloid malignancies, often due to mutations in splicing factors.
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