Au-24 as a potential thioredoxin reductase inhibitor in hepatocellular carcinoma cells

Gaopan Dong1, Xiaohan Ye2, Shumei Wang3

  • 1Key Laboratory of Chemical Biology (MOE), School of Pharmaceutical Sciences, Cheeloo College of Medicine, Shandong University, Jinan, Shandong 250012, China; School of Pharmacy, Xinxiang Medical University, Xinxiang, Henan 453003, China.

Pharmacological Research
|February 6, 2022
PubMed

Insights

A novel thioredoxin reductase (TrxR) inhibitor, Au-24, effectively suppressed hepatocellular carcinoma (HCC) cell proliferation and tumor growth in vitro and in vivo. Au-24 shows promise for HCC treatment by inducing oxidative stress and apoptosis.

Area of Science:

  • Biochemistry
  • Oncology
  • Pharmacology

Background:

  • Hepatocellular carcinoma (HCC) remains a significant global health challenge.
  • Thioredoxin reductase (TrxR) is a key enzyme implicated in cancer cell survival and proliferation.
  • Targeting TrxR presents a potential therapeutic strategy for HCC.

Purpose of the Study:

  • To investigate the inhibitory potential of a novel TrxR inhibitor, Au-24, against hepatocellular carcinoma (HCC).
  • To evaluate the efficacy of Au-24 in both in vitro and in vivo HCC models.

Main Methods:

  • In vitro studies utilized HepG2 cells to assess Au-24's effects on proliferation, mitochondrial membrane potential (MMP), reactive oxygen species (ROS) levels, DNA damage, autophagy, cell cycle, and apoptosis.
  • The impact of Au-24 on key signaling pathways including apoptosis, MAPK, PI3K/AKT/mTOR, NF-κB, and STAT3 was examined.
  • In vivo experiments involved implanting HepG2 tumors and comparing the efficacy of Au-24 with AA1, assessing tumor growth, Ki67, CD31 expression, apoptosis, and necrosis.

Main Results:

  • Au-24 suppressed HepG2 cell proliferation by reducing MMP and increasing ROS, leading to oxidative stress, DNA damage, autophagy, cell cycle arrest, and apoptosis.
  • Au-24 modulated apoptosis, MAPK, PI3K/AKT/mTOR, NF-κB, and STAT3 signaling pathways.
  • In vivo, Au-24 demonstrated superior inhibition of HepG2 tumor growth compared to AA1, evidenced by decreased Ki67 and CD31 expression and increased tumor cell apoptosis and necrosis.

Conclusions:

  • Au-24 exhibits potent anti-cancer activity against hepatocellular carcinoma (HCC) through mechanisms involving oxidative stress induction and apoptosis.
  • The compound effectively inhibits tumor growth in vivo, suggesting its therapeutic potential.
  • Au-24 represents a promising TrxR inhibitor candidate for the treatment of HCC.