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Update of treatment for Gaucher disease

Weijing Kong1, Cheng Lu2, Yingxue Ding1

  • 1Department of Pediatrics, Beijing Friendship Hospital, Capital Medical University, Beijing, 100050, China.

European Journal of Pharmacology
|May 15, 2022
PubMed

Keywords:
Enzyme replacement therapyGaucher diseaseGene therapyGenome editingHematopoietic stem cell transplantationSubstrate reduction therapy

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