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Updated: Sep 22, 2025

Identification and Classification of Position-specific GABAA Receptor Subunit Missense Variants for Their Role In Hippocampal Pyramidal Neurons
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Identification and Classification of Position-specific GABAA Receptor Subunit Missense Variants for Their Role In Hippocampal Pyramidal Neurons

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Gene-based therapeutics for rare genetic neurodevelopmental psychiatric disorders

Beverly L Davidson1, Guangping Gao2, Elizabeth Berry-Kravis3

  • 1Raymond G. Perelman Center for Cellular and Molecular Therapeutics, The Children's Hospital of Philadelphia, Philadelphia, PA, USA; Department of Pathology and Laboratory Medicine, University of Pennsylvania, Philadelphia, PA, USA.

Molecular Therapy : the Journal of the American Society of Gene Therapy
|May 19, 2022
PubMed

Keywords:
gene therapyneurodevelopmentpsychiatric disorders

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